80 Diseases Treated  by Stem Cells


Diseases That Can Be Treated by Stem Cell Transplantation





 







Stem Cell Disorders

  • Aplastic Anemia (Severe)
  • Fanconi Anemia
  • Paroxysmal Nocturnal Hemoglobinuria (PNH)

Acute Leukemias

  • Acute Lymphoblastic Leukemia (ALL)
  • Acute Myelogenous Leukemia (AML)
  • Acute Biphenotypic Leukemia
  • Acute Undifferentiated Leukemia

Chronic Leukemias

  • Chronic Myelogenous Leukemia (CML)
  • Chronic Lymphocytic Leukemia (CLL)
  • Juvenile Chronic Myelogenous Leukemia (JCML)
  • Juvenile Myelomonocytic Leukemia (JMML)

Myeloproliferative Disorders

  • Acute Myelofibrosis
  • Agnogenic Myeloid Metaplasia (myelofibrosis)
  • Polycythemia Vera
  • Essential Thrombocythemia


Myelodysplastic Syndromes

  • Refractory Anemia (RA)
  • Refractory Anemia with Ringed Sideroblasts (RARS)
  • Refractory Anemia with Excess Blasts (RAEB)
  • Refractory Anemia with Excess Blasts in Transformation (RAEB-T)
  • Chronic Myelomonocytic Leukemia (CMML)

Lymphoproliferative Disorders

  • Non-Hodgkin’s Lymphoma
  • Hodgkin’s Disease
  • Prolymphocytic Leukemia

Inherited Erythrocyte Abnormalities

  • Beta Thalassemia Major
  • Pure Red Cell Aplasia
  • Sickle Cell Disease
     

Liposomal Storage Diseases

  • Mucopolysaccharidoses (MPS)
  • Hurler Syndrome (MPS-IH)
  • Scheie Syndrome (MPS-IS)
  • Hunter’s Syndrome (MPS-II)
  • Sanfilippo Syndrome (MPS-III)
  • Morquio Syndrome (MPS-IV)
  • Maroteaux-Lamy Syndrome (MPS-VI)
  • Sly Syndrome, Beta-Glucuronidase Deficiency (MPS-VII)
  • Adrenoleukodystrophy
  • Mucolipidosis II (I-cell Disease)
  • Krabbe Disease
  • Gaucher’s Disease
  • Niemann-Pick Disease
  • Wolman Disease
  • Metachromatic Leukodystrophy


Histiocytic Disorders

  • Familial Erythrophagocytic Lymphohistiocytosis
  • Histiocytosis-X
  • Hemophagocytosis

Phagocyte Disorders

  • Chediak-Higashi Syndrome
  • Chronic Granulomatous Disease
  • Neutrophil Actin Deficiency
  • Reticular Dysgenesis

Congenital Immune System Disorders

  • Ataxia-Telangiectasia
  • Kostmann Syndrome
  • Leukocyte Adhesion Deficiency
  • DiGeorge Syndrome
  • Bare Lymphocyte Syndrome
  • Omenn’s Syndrome
  • Severe Combined Immunodeficiency (SCID)
  • SCID with Adenosine Deaminase Deficiency
  • Absence of T & B Cells SCID
  • Absence of T Cells, Normal B Cell SCID
  • Common Variable Immunodeficiency
  • Wiskott-Aldrich Syndrome
  • X-Linked Lymphoproliferative Disorder

Inherited Platelet Abnormalities

  • Amegakaryocytosis / Congenital Thrombocytopenia

Plasma Cell Disorders

  • Multiple Myeloma
  • Plasma Cell Leukemia
  • Waldenstrom’s Macroglobulinemia

Other Inherited Disorders

  • Lesch-Nyhan Syndrome
  • Cartilage-Hair Hypoplasia
  • Glanzmann Thrombasthenia
  • Osteopetrosis

Other Malignancies

  • Breast Cancer
  • Ewing Sarcoma
  • Neuroblastoma
  • Renal Cell Carcinoma

 

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